Gene therapy for Friedreich ataxia: Too much, too little, or just right?
dc.contributor.author | Payne, R. Mark | |
dc.contributor.department | Pediatrics, School of Medicine | en_US |
dc.date.accessioned | 2023-05-18T12:46:53Z | |
dc.date.available | 2023-05-18T12:46:53Z | |
dc.date.issued | 2022-03-04 | |
dc.eprint.version | Final published version | en_US |
dc.identifier.citation | Payne RM. Gene therapy for Friedreich ataxia: Too much, too little, or just right?. Mol Ther Methods Clin Dev. 2022;25:1-2. Published 2022 Mar 4. doi:10.1016/j.omtm.2022.02.008 | en_US |
dc.identifier.uri | https://hdl.handle.net/1805/33096 | |
dc.language.iso | en_US | en_US |
dc.publisher | Elsevier | en_US |
dc.relation.isversionof | 10.1016/j.omtm.2022.02.008 | en_US |
dc.relation.journal | Molecular Therapy: Methods & Clinical Development | en_US |
dc.rights | Attribution-NonCommercial-NoDerivatives 4.0 International | * |
dc.rights.uri | http://creativecommons.org/licenses/by-nc-nd/4.0/ | * |
dc.source | PMC | en_US |
dc.subject | Friedreich ataxia | en_US |
dc.subject | Mitochondria | en_US |
dc.subject | Monogenetic diseases | en_US |
dc.subject | Viral gene therapies | en_US |
dc.title | Gene therapy for Friedreich ataxia: Too much, too little, or just right? | en_US |
dc.type | Article | en_US |