Gene therapy for Friedreich ataxia: Too much, too little, or just right?

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Date
2022-03-04
Authors
Payne, R. Mark
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American English
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Pediatrics, School of Medicine
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Elsevier
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Friedreich ataxia, Mitochondria, Monogenetic diseases, Viral gene therapies
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Payne RM. Gene therapy for Friedreich ataxia: Too much, too little, or just right?. Mol Ther Methods Clin Dev. 2022;25:1-2. Published 2022 Mar 4. doi:10.1016/j.omtm.2022.02.008
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Molecular Therapy: Methods & Clinical Development
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Attribution-NonCommercial-NoDerivatives 4.0 International Creative Commons licenses
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PMC
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https://hdl.handle.net/1805/33096
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https://doi.org/10.1016/j.omtm.2022.02.008
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