Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on In Vitro Experimental Evidence
dc.contributor.author | Huang, Yunjie | |
dc.contributor.author | Paul, Grace | |
dc.contributor.author | Lee, Jesun | |
dc.contributor.author | Yarlagadda, Sunitha | |
dc.contributor.author | McCoy, Karen | |
dc.contributor.author | Naren, Anjaparavanda P. | |
dc.contributor.department | Pediatrics, School of Medicine | |
dc.date.accessioned | 2024-09-23T13:53:32Z | |
dc.date.available | 2024-09-23T13:53:32Z | |
dc.date.issued | 2021 | |
dc.eprint.version | Final published version | |
dc.identifier.citation | Huang Y, Paul G, Lee J, Yarlagadda S, McCoy K, Naren AP. Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on In Vitro Experimental Evidence. Am J Respir Crit Care Med. 2021;204(10):1231-1235. doi:10.1164/rccm.202101-0090LE | |
dc.identifier.uri | https://hdl.handle.net/1805/43516 | |
dc.language.iso | en_US | |
dc.publisher | American Thoracic Society | |
dc.relation.isversionof | 10.1164/rccm.202101-0090LE | |
dc.relation.journal | American Journal of Respiratory and Critical Care Medicine | |
dc.rights | Publisher Policy | |
dc.source | PMC | |
dc.subject | Aminophenols | |
dc.subject | Benzodioxoles | |
dc.subject | Cystic fibrosis transmembrane conductance regulator | |
dc.subject | Gene expression regulation | |
dc.subject | Pyrazoles | |
dc.subject | Pyrrolidines | |
dc.subject | Quinolones | |
dc.title | Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on In Vitro Experimental Evidence | |
dc.type | Article | |
ul.alternative.fulltext | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC8759307/ |