Li, ShuangZhang, ChenHan, Renzhi2025-05-142025-05-142025-03-19Li S, Zhang C, Han R. An oversized AAV8 vector to deliver CPS1. Mol Ther Nucleic Acids. 2025;36(2):102504. Published 2025 Mar 19. doi:10.1016/j.omtn.2025.102504https://hdl.handle.net/1805/48072en-USAttribution-NonCommercial-NoDerivatives 4.0 InternationalCarbamoyl phosphate synthetase 1 (CPS1) deficiencyUrea cycle disordersHyperammonemiaComaDeathArticle