Gene therapy for Friedreich ataxia: Too much, too little, or just right?

Payne, R. Mark2023-05-182023-05-182022-03-04Payne RM. Gene therapy for Friedreich ataxia: Too much, too little, or just right?. Mol Ther Methods Clin Dev. 2022;25:1-2. Published 2022 Mar 4. doi:10.1016/j.omtm.2022.02.008https://hdl.handle.net/1805/33096en-USAttribution-NonCommercial-NoDerivatives 4.0 InternationalFriedreich ataxiaMitochondriaMonogenetic diseasesViral gene therapiesGene therapy for Friedreich ataxia: Too much, too little, or just right?Article